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  • Publication

BIO-Europe 2025: AAVantgarde Bio, which is working on gene therapies for inherited retinal diseases that are caused by mutations in large genes, closed a $141M series B raise today

  • Publication
  • Stargardt

Retinal gene therapy for Stargardt disease with dual AAV intein vectors is both safe and effective in large animal models

  • Publication
  • Usher 1B

Efficacy, pharmacokinetics, and safety in the mouse and primate retina of dual AAV vectors for Usher syndrome type 1B

  • Publication
  • Stargardt

Intein-mediated protein trans-splicing expands adeno-associated virus transfer capacity in the retina

  • Publication
  • Other

Efficient gene delivery to the cone-enriched pig retina by dual AAV vectors

  • Publication
  • Other

Effective delivery of large genes to the retina by dual AAV vectors