Pioneering large gene delivery to improve the lives of patients with debilitating diseases
Our mission
Gene Therapy based on Adeno-Associated Viral (AAV) vectors has proven to be transformative in the treatment of genetic illnesses, however, the small vector payload limits their further application.
The AAVantgarde cutting-edge gene therapy technology platforms are focused on solving the constraint of oversized gene delivery, with our technologies opening up the opportunity for genetic medicine delivery to more underserved patients with debilitating diseases.
Delivering the next generation of gene therapies
Focused on broadening the application of AAV-based gene therapies.
Advancing our platforms
Our pipeline addresses IRDs with high unmet need and we have the potential to expand to other therapeutic areas with our technology
AAV gene therapy has been limited by transgene capacity, and AAVantgarde’s proprietary platforms enable delivery of large genes to tissue and cells in vivo; something that could extend into many disease areas”